STAT August 6, 2024
Roche, the Swiss pharmaceutical giant, earlier this year abruptly cancelled an international clinical trial of a drug being studied to treat children with a rare genetic disorder, citing “trade-offs made … to increase the overall portfolio value.”
The news stunned parents of children enrolled in the Phase 2 study, as well as the academic researchers running it. Shannon Sadecki, whose son was in the trial, said she felt like she’d been “hit by...