Forbes August 8, 2024
New gene editing techniques, like adenine base editing and prime editing, are creating new possibilities for treating dilated cardiomyopathy, a heart condition affecting about 1 in 250 people worldwide. It is also a leading cause of heart failure and sudden cardiac death. In a recent study, advanced techniques were used to fix mutations in the RNA binding motif protein 20 (RBM20) gene, a common factor in familial dilated cardiomyopathy. The study showed promising results in improving heart function and extending lifespan in mice.
Gene Therapy for Dilated Cardiomyopathy
The study aimed to assess the effectiveness of adenine base editing and prime editing in correcting mutations and their impact on heart function. Think of it as using a molecular eraser and...
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