AJMC February 14, 2025
Key Takeaways
- CGTs present significant challenges across diagnosis, treatment, and post-treatment stages, requiring coordinated stakeholder efforts to streamline processes and reduce barriers.
- Early diagnosis and treatment are critical, with expanded newborn screening and novel genetic tests simplifying CGT access.
- Financial burdens and logistical challenges post-diagnosis necessitate innovative payment models and infrastructure improvements, like the “hub-and-spoke” model.
- Comprehensive support systems, including personal relationships, travel benefits, and care navigation, are essential for optimizing patient and caregiver experiences.
Cell and gene therapies can be life-changing for patients with certain conditions, but the process of receiving them poses barriers for patients and caregivers that require multistakeholder solutions, according to a white paper from the National Pharmaceutical Council.
While cell and gene therapies...
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