Forbes July 25, 2024
William A. Haseltine

What if we could repair fundamental parts of our bodies? Gene therapy promises just that. It’s like having a molecular mechanic that can fix or replace faulty genes, potentially curing diseases previously thought to be incurable. One area where gene therapy is making significant progress is in treating blood disorders. It offers hope to people with sickle cell disease or hemophilia.

More recently, we have even seen success in implementing therapies directly in the body, a process known as in vivo gene editing. It’s like performing microsurgery on your DNA while it’s still inside you. This approach could open doors to treating many diseases with a single procedure. One study recognized and explored the potential of this in vivo therapy...

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