pharmaphorum July 19, 2024
The FDA has said it will create a rare disease innovation hub to help speed the development of new treatments and build connections between developers and the rare disease community.
The hub will focus in particular on diseases that affect very small patient populations and those where the disease mechanisms are not fully understood, according to the US regulator. It will be co-led by Patrizia Cavazzoni, director of the FDA’s Centre for Drugs Evaluation and Research (CDER), and Centre for Biologics Evaluation and Research (CBER) director Peter Marks.
In a joint statement, Cavazzoni and Marks noted that more than half of all the novel drugs and biologics approved by the FDA last year were to prevent, diagnose or treat a...
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