Inside Precision Medicine June 4, 2024
Julia Vitarello is on a personal mission to open up access to individualized therapies for people with rare diseases, starting in the U.K. with the government-backed Rare Therapies Launch Pad
In recent years, whole genome sequencing has made it easier to diagnose rare genetic diseases while scientific advances have put individualized treatments within reach. Yet, the regulatory processes, typically designed for large-scale drug production, are lagging behind. This, combined with limited funding and a lack of awareness, makes it painfully difficult for people with rare diseases to access the life-saving therapies they so desperately need. Julia Vitarello is hoping to change this.
Mila’s story
Ten years ago, Julia had very little knowledge of genetic diseases, she also had no idea...
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