Fierce Biotech December 11, 2023
On the heels of Friday’s FDA approval of not one but two gene therapies to treat sickle cell disease (SCD), Editas Medicine is sharing another slice of early data for its gene-edited candidate designed to tackle the same condition.
The new data span 17 patients who received Edita’s renizgamglogene autogedtemcel (reni-cel), either in a phase 1/2 trial dubbed RUBY for severe SCD or in a separate phase 1/2 trial known as EdiTHAL for transfusion-dependent beta thalassemia (TDT). The results build off a previous dataset shared this summer, incorporating information from 12 more patients, and were presented on Dec. 11 at the 65th American Society of Hematology Annual Meeting and Exposition.
The gene-editing biotech assessed lead candidate reni-cel among 11...
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